Duchenne Muscular Dystrophy (DMD) is the most common form of muscular dystrophy characterised by progressive skeletal muscle degeneration and weakness....
Rare
Myasthenia gravis (MG) is a rare neuromuscular disorder that affects the transmission of signals between nerves and muscles. It is...
A new hope is looming for Myelofibrosis patients who experienced a suboptimal response to ruxolitinib and those who were JAK...
Emirates Oncology Society (EOS) and Ipsen joined forces to raise awareness of Neuroendocrine Tumors (NET), a rare type of cancer....
Several indications and molecules were approved in July by FDA including the following: Asparaginase erwinia chrysanthemi (recombinant)-rywn) as a component...
What is Wilson's disease? Wilson's disease is a rare genetic autosomal disease. It occurs in approximately one in 30,000 to 40,000...
Calciphylaxis is an uncommon, rare, serious, and fatal disorder that is characterized by: Calcification of the small blood vessels...
Char syndrome is a rare, genetic, multiple congenital anomalies/dysmorphic syndrome characterized by: Triad of patent ductus arteriosus (PDA) Typical facial...
Anaplastic large-cell lymphoma (ALCL) is a rare type of non-Hodgkin lymphoma that T-cells. Pathologically, T-cells appear abnormal, large, and undeveloped. Most patients are...
Hypopituitarism is a rare disorder where the pituitary gland stops make enough hormones. Hormones produced by the pituitary gland are...
